Oral Epalrestat Therapy in Pediatric Subjects With PMM2-CDG – Maggie’s Pearl, LLC Active, not recruiting The objective is to assess the safety, tolerability, and clinical and metabolic improvement of pediatric subjects with PMM2-CDG on oral epalrestat therapy. This is a prospective, single-center, randomized, double-blind, placebo-controlled study designed to assess the safety, tolerability, and clinical and metabolic … Continue reading Clinical Trials